2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| congenital | ceruloplasmin | Orphan Designation | - |
| congenital adrenal hyperplasia | ceruloplasmin | Orphan Designation | - |
| congenital heart disease | ceruloplasmin | Orphan Designation | - |
| ligneous conjunctivitis | human plasminogen | Orphan Designation | - |