1
Orphan Designations
0 approved, 1 designated
0
FDA Approvals
1
Active Trials
200 recruiting
2
Rare Diseases
across 2 areas
0
News (30d)
Quiet
KIND Pharmaceuticals LLC is a company with 1 orphan drug designation across 2 rare diseases. Active clinical trials in 1 indication. gene therapy candidates in 1 disease. 19 active policy bills affect their portfolio.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| sickle cell disease | (8'-hydroxy-6'-oxo-3'-phenyl-6'H-spiro[cyclopentyl-1,5'-indolazine]-7'-carbonyl) glycine | Des.TrialAppr. |
| thalassemia | - | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
16
overlap in 2+ diseases
1/2
candidate diseases
0
avg importance: 0
19
affecting portfolio
0% of portfolio targets high unmet need diseases
16
overlap in 2+ diseases
1/2
candidate diseases
0
avg importance: 0
19
affecting portfolio