1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| diffuse idiopathic pulmonary neuroendocrine cell hyperplasia | 1,2:5,6-dianhydrogalactitol | Orphan Designation | - |
| diffuse intrinsic pontine glioma | 1,2:5,6-dianhydrogalactitol | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 6 (hepatocerebral type) | 1,2:5,6-dianhydrogalactitol | Orphan Designation | - |