1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| bronchial endocrine tumor | AAV2.adalimumab | Orphan Designation | - |
| recessive dystrophic epidermolysis bullosa-generalized other | AAV2.adalimumab | Orphan Designation | - |
| thymic neuroendocrine tumor | AAV2.adalimumab | Orphan Designation | - |