4
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| B-cell chronic lymphocytic leukemia | entospletinib | Orphan Designation | - |
| acute myeloid leukemia | lanraplenibentospletinib | Orphan Designation | - |
| chronic graft versus host disease | entospletinib | Orphan Designation | - |
| chronic inflammatory demyelinating polyradiculoneuropathy | entospletinib | Orphan Designation | - |
| chronic primary adrenal insufficiency | entospletinib | Orphan Designation | - |