3
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| B-cell adult acute lymphocytic leukemia | mogamulizumab | Orphan Designation | - |
| H syndrome | POTELIGEO | Orphan Designation | - |
| T-cell adult acute lymphocytic leukemia | mogamulizumab | Orphan Designation | - |
| adult T-cell leukemia/lymphoma | mogamulizumab | Orphan Designation | - |
| adult neuronal ceroid lipofuscinosis | POTELIGEO | Orphan Designation | - |
| adult pleomorphic rhabdomyosarcoma | POTELIGEO | Orphan Designation | - |
| adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia | POTELIGEO | Orphan Designation | - |
| fanconi anemia, complementation group 10 | POTELIGEO | Orphan Designation | - |
| mature T-cell and NK-cell non-Hodgkin lymphoma | mogamulizumab | Orphan Designation | - |
| primary adult heart tumor | POTELIGEO | Orphan Designation | - |