3
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Angelman syndrome | human gammaglobulin | Orphan Designation | - |
| acquired idiopathic inflammatory myopathy | human gammaglobulin | Orphan Designation | - |
| alobar holoprosencephaly | human gammaglobulin | Orphan Designation | - |
| intellectual disability, autosomal dominant 54 | human gammaglobulin | Orphan Designation | - |
| lobar holoprosencephaly | human gammaglobulin | Orphan Designation | - |
| malignant carotid body paraganglioma | human gammaglobulin | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 6 (hepatocerebral type) | human gammaglobulin | Orphan Designation | - |
| post-treatment Lyme disease syndrome | human gammaglobulin | Orphan Designation | - |
| solitary rectal ulcer syndrome | human gammaglobulin | Orphan Designation | - |
| treatment-refractory schizophrenia | human gammaglobulin | Orphan Designation | - |