3
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| idiopathic pulmonary fibrosis | ESBRIET | Orphan Designation | - |
| limited systemic sclerosis | pirfenidone | Orphan Designation | - |
| mediastinal gray zone lymphoma | pirfenidone | Orphan Designation | - |
| myelodysplastic syndrome | pirfenidone | Orphan Designation | - |
| myeloproliferative neoplasm, unclassifiable | pirfenidone | Orphan Designation | - |
| pulmonary systemic sclerosis | pirfenidone | Orphan Designation | - |
| systemic sclerosis | pirfenidone | Orphan Designation | - |