5
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| IgA glomerulonephritis | GCSF-mobilized autologous CD34 cells for intramuscular injection | Orphan Designation | - |
| cholangiocarcinoma | certepetide | Orphan Designation | - |
| malignant glioma | certepetide | Orphan Designation | - |
| malignant pancreatic neoplasm | certepetide | Orphan Designation | - |
| osteosarcoma | certepetide | Orphan Designation | - |
| pernicious anemia | GCSF-mobilized autologous CD34 cells for intramuscular injection | Orphan Designation | - |
| thromboangiitis obliterans | GCSF-mobilized autologous CD34 cells for intramuscular injection | Orphan Designation | - |