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Loxo Oncology, Inc., a wholly owned subsidiary of Eli Lilly and Company — Rare Disease Pipeline | Kisho | Kisho
Loxo Oncology, Inc., a wholly owned subsidiary of Eli Lilly and Company
Other
4
Orphan Designations
0
FDA Approvals
15
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
RET fusion positive cancer
RETEVMO
Retevmo
Orphan Designation
-
adult neuronal ceroid lipofuscinosis
Jaypirca
Orphan Designation
-
adult pleomorphic rhabdomyosarcoma
Jaypirca
Retevmo
Orphan Designation
-
adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia
Retevmo
Jaypirca
Orphan Designation
-
adult-onset proximal spinal muscular atrophy, autosomal dominant
Jaypirca
Orphan Designation
-
autosomal dominant myopia-midfacial retrusion-sensorineural hearing loss-rhizomelic dysplasia syndrome
RETEVMO
Orphan Designation
-
chronic lymphocytic leukemia/small lymphocytic lymphoma
Jaypirca
Orphan Designation
-
familial scaphocephaly syndrome, McGillivray type
RETEVMO
Retevmo
Orphan Designation
-
micrognathia-recurrent infections-behavioral abnormalities-mild intellectual disability syndrome
RETEVMO
Retevmo
Orphan Designation
-
muscle tissue disorder
Retevmo
Orphan Designation
-
primary adult heart tumor
Jaypirca
Retevmo
Orphan Designation
-
soft tissue amyloid neoplasm
Retevmo
Orphan Designation
-
soft tissue chondroma
Retevmo
Orphan Designation
-
soft tissue sarcoma
Retevmo
Orphan Designation
-
tumor of adipose tissue
Retevmo
Orphan Designation
-
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