1
Orphan Designations
0 approved, 1 designated
0
FDA Approvals
0
Active Trials
200 recruiting
5
Rare Diseases
across 9 areas
0
News (30d)
Quiet
Maas Biolab,LLC is a company with 1 orphan drug designation across 5 rare diseases.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| BCOR ITD sarcoma | Cyclosporin A | Des.TrialAppr. |
| Ito hypomelanosis | Cyclosporin A | Des.TrialAppr. |
| amyotrophic lateral sclerosis | Cyclosporin A | Des.TrialAppr. |
| nevus of Ito | Cyclosporin A | Des.TrialAppr. |
| tarsal tunnel syndrome | Cyclosporin A | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
1
overlap in 2+ diseases
0/5
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
1
overlap in 2+ diseases
0/5
candidate diseases
0
avg importance: 0
0
affecting portfolio