2
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Kabuki syndrome 1 | margetuximab | Orphan Designation | - |
| Smith-Lemli-Opitz syndrome | margetuximab | Orphan Designation | - |
| acute myeloid leukemia | flotetuzumab | Orphan Designation | - |
| gastric leiomyosarcoma | margetuximab | Orphan Designation | - |
| gastric lymphoma | margetuximab | Orphan Designation | - |
| gastric ulcer | margetuximab | Orphan Designation | - |
| gastric volvulus, intrathoracic | margetuximab | Orphan Designation | - |