5
Orphan Designations
0
FDA Approvals
12
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| 15q11q13 microduplication syndrome | Nitric oxide | Orphan Designation | - |
| Marfan syndrome | Nitric oxide | Orphan Designation | - |
| arteriovenous malformations of the brain | Nitric oxide | Orphan Designation | - |
| hepatorenal syndrome | Terlivaz | Orphan Designation | - |
| hypotonia-failure to thrive-microcephaly syndrome | Terlivaz | Orphan Designation | - |
| idiopathic pulmonary fibrosis | drug component, inhaled nitric oxide, of the inhaled nitric oxice/INOpulse® Device combination product | Orphan Designation | - |
| insensitivity to pain with hyperplastic Myelinopathy | Terlivaz | Orphan Designation | - |
| pulmonary arterial hypertension | nitric oxide | Orphan Designation | - |
| sickle cell disease | nitric oxide | Orphan Designation | - |
| sickle cell-hemoglobin c disease syndrome | nitric oxide | Orphan Designation | - |
| sickle cell-hemoglobin d disease syndrome | nitric oxide | Orphan Designation | - |
| twin to twin transfusion syndrome | Terlivaz | Orphan Designation | - |