4
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| cholecystitis | Trimetazidine | Orphan Designation | - |
| chronic beryllium disease | Trimetazidine | Orphan Designation | - |
| dilated cardiomyopathy | trimetazidine | Orphan Designation | - |
| lethal congenital glycogen storage disease of heart | docarpamine | Orphan Designation | - |
| pulmonary arterial hypertension | trimetazidine | Orphan Designation | - |
| respiratory failure | Trimetazidine | Orphan Designation | - |