1
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| atrial fibrillation, familial, 1 | M.V.I.-12 | Orphan Designation | - |
| atrial fibrillation, familial, 3 | M.V.I.-12 | Orphan Designation | - |
| chronic thromboembolic pulmonary hypertension | M.V.I.-12 | Orphan Designation | - |
| hereditary hypercarotenemia and vitamin A deficiency | M.V.I.-12 | Orphan Designation | - |
| hypercarotenemia and vitamin A deficiency, autosomal recessive | M.V.I.-12 | Orphan Designation | - |
| inborn disorder of cobalamin metabolism and transport | M.V.I.-12 | Orphan Designation | - |
| methylmalonic aciduria and homocystinuria type cblC | M.V.I.-12 | Orphan Designation | - |
| vitamin B12-responsive methylmalonic acidemia | M.V.I.-12 | Orphan Designation | - |
| vitamin deficiency disorder | M.V.I.-12 | Orphan Designation | - |