2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| glioma | liposomal gadodiamide | Orphan Designation | - |
| glioma susceptibility 4 | liposomal topotecan hydrochloride | Orphan Designation | - |
| mixed glioma | liposomal topotecan hydrochloride | Orphan Designation | - |
| optic pathway glioma | liposomal topotecan hydrochloride | Orphan Designation | - |