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Medicis Pharmaceutical Corp. — Rare Disease Pipeline | Kisho | Kisho
Medicis Pharmaceutical Corp.
Other
3
Orphan Designations
0
FDA Approvals
16
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
Susac syndrome
Ammonul
Orphan Designation
-
anti-glomerular basement membrane disease
Buphenyl
Orphan Designation
-
argininosuccinic aciduria
Buphenyl
Orphan Designation
-
citrullinemia type I
Buphenyl
Orphan Designation
-
citrullinemia, type II, adult-onset
Buphenyl
Orphan Designation
-
congenital lethal erythroderma
sodium phenylbutyrate
Orphan Designation
-
karyomegalic interstitial nephritis
Buphenyl
Orphan Designation
-
malignant carotid body paraganglioma
sodium phenylbutyrate
Orphan Designation
-
neurodegeneration with brain iron accumulation 5
Ammonul
Orphan Designation
-
post 5-alpha-reductase inhibitors treatment syndrome
sodium phenylbutyrate
Orphan Designation
-
post-treatment Lyme disease syndrome
sodium phenylbutyrate
Orphan Designation
-
sickle cell-beta-thalassemia disease syndrome
sodium phenylbutyrate
Orphan Designation
-
steroid-responsive encephalopathy associated with autoimmune thyroiditis
Ammonul
Orphan Designation
-
treatment-refractory schizophrenia
sodium phenylbutyrate
Orphan Designation
-
urea cycle disorder
Buphenyl
Orphan Designation
-
urea cycle disorder or inherited hyperammonemia
Buphenyl
Orphan Designation
-
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