1
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Young syndrome | Respigam | Orphan Designation | - |
| nut midline carcinoma | Respigam | Orphan Designation | - |
| primary microcephaly-mild intellectual disability-young-onset diabetes syndrome | Respigam | Orphan Designation | - |
| respiratory failure | Respigam | Orphan Designation | - |
| respiratory or thoracic malformation | Respigam | Orphan Designation | - |
| respiratory syncytial virus bronchiolitis | Respigam | Orphan Designation | - |
| respiratory syncytial virus infectious disease | Respigam | Orphan Designation | - |
| respiratory system benign neoplasm | Respigam | Orphan Designation | - |
| serous surface papilloma | Respigam | Orphan Designation | - |
| young-onset Parkinson disease | Respigam | Orphan Designation | - |