4
Orphan Designations
0 approved, 3 designated
0
FDA Approvals
1
Active Trials
200 recruiting
5
Rare Diseases
across 7 areas
0
News (30d)
Quiet
MedPacto, Inc. is a company with 4 orphan drug designations across 5 rare diseases. Active clinical trials in 1 indication.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| gastric cancer | Vactosertib | Des.TrialAppr. |
| hepatocellular carcinoma | N-((4-([1,2,4]triazolo[1,5-a]pyridin-6-yl)-5-(6-methylpyridin-2-yl)-1H-imidazol-2-yl)methyl)-2-fluoroaniline | Des.TrialAppr. |
| malignant pancreatic neoplasm | Vactosertib | Des.TrialAppr. |
| osteosarcoma | vactosertib | Des.TrialAppr. |
| sarcoma | - | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
64
overlap in 2+ diseases
0/5
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
64
overlap in 2+ diseases
0/5
candidate diseases
0
avg importance: 0
0
affecting portfolio