1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Pelizaeus-Merzbacher disease in female carriers | Allogeneic cytomegalovirus cytotoxic T lymphocytes | Orphan Designation | - |
| Pick disease | Allogeneic cytomegalovirus cytotoxic T lymphocytes | Orphan Designation | - |
| alpha-mannosidosis | Allogeneic cytomegalovirus cytotoxic T lymphocytes | Orphan Designation | - |
| cytomegalovirus pneumonia | Allogeneic cytomegalovirus cytotoxic T lymphocytes | Orphan Designation | - |
| cytomegalovirus retinitis | Allogeneic cytomegalovirus cytotoxic T lymphocytes | Orphan Designation | - |
| idiopathic disseminated cytomegalovirus infection | Allogeneic cytomegalovirus cytotoxic T lymphocytes | Orphan Designation | - |