1
Orphan Designations
2
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| X-linked parkinsonism-spasticity syndrome | OZOBAX | Orphan Designation | - |
| chronic hiccup | OZOBAX | Orphan Designation | - |
| diffuse cerebral and cerebellar atrophy - intractable seizures - progressive microcephaly syndrome | OZOBAX | Orphan Designation | - |
| intractable diarrhea-choanal atresia-eye anomalies syndrome | OZOBAX | Orphan Designation | - |
| myoclonus, intractable, neonatal | OZOBAX | Orphan Designation | - |
| refractory celiac disease | OZOBAX | Orphan Designation | - |