1
Orphan Designations
0
FDA Approvals
1
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| pulmonary non-tuberculous mycobacterial infection | (S)-3-(((S)-3-(aminomethyl)-1-hydroxy-1,3- dihydrobenzo[c][1,2]oxaborol-7-yl)oxy)propane-1,2-diyl bis(2-methylpropanoate) hydrochloride | Orphan Designation | - |