2
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Pearson syndrome | autologous CD34+ Cells Enriched with Blood Derived Mitochondria | Orphan Designation | - |
| myelodysplastic syndrome | patient-derived autologous CD34+ hematopoietic stem and progenitor cells (HSPCs) mobilized from peripheral blood and enriched with exogenous mitochondria from an allogeneic placenta | Orphan Designation | - |