4
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute myeloid leukemia | liposomal annamycin | Orphan Designation | - |
| alveolar soft part sarcoma | liposomal annamycin | Orphan Designation | - |
| glioblastoma | (E)-3-(6-Bromo-pyridin-2-yl)-2-cyano-N-((S)-1-phenyl-ethyl)-acryl amide | Orphan Designation | - |
| glioma susceptibility 1 | an acetic acid diester of 2-deoxy-D-glucose | Orphan Designation | - |
| soft tissue sarcoma | liposomal annamycin | Orphan Designation | - |
| undifferentiated pleomorphic sarcoma | liposomal annamycin | Orphan Designation | - |