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MSD International Business GmbH — Rare Disease Pipeline | Kisho | Kisho
MSD International Business GmbH
Other
10
Orphan Designations
0
FDA Approvals
43
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
Bicervical bicornuate uterus with patent cervix and vagina
Keytruda
Orphan Designation
-
Char syndrome
Keytruda
Orphan Designation
-
Cryoglobulinemic vasculitis
Keytruda
Orphan Designation
-
Hodgkins lymphoma
Keytruda
Orphan Designation
-
MALT lymphoma
Keytruda
Orphan Designation
-
adult embryonal tumor with multilayered rosettes, c19mc-altered
Keytruda
Orphan Designation
-
adult hepatocellular carcinoma
Keytruda
Orphan Designation
-
adult neuronal ceroid lipofuscinosis
Keytruda
Orphan Designation
-
adult pleomorphic rhabdomyosarcoma
Keytruda
Orphan Designation
-
adult-onset chronic progressive external ophthalmoplegia with mitochondrial myopathy
Keytruda
Orphan Designation
-
adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia
Keytruda
Orphan Designation
-
adult-onset proximal spinal muscular atrophy, autosomal dominant
Keytruda
Orphan Designation
-
carbon monoxide-induced delayed encephalopathy
Keytruda
Orphan Designation
-
carcinoma of esophagus
Keytruda
Orphan Designation
-
cataract 13 with adult I phenotype
Keytruda
Orphan Designation
-
deafness, congenital, and adult-onset progressive leukoencephalopathy
Keytruda
Orphan Designation
-
distal biliary tract carcinoma
Keytruda
Orphan Designation
-
fibrolamellar hepatocellular carcinoma
Keytruda
Orphan Designation
-
gastric cancer
Keytruda
Orphan Designation
-
hepatocellular carcinoma
Keytruda
Orphan Designation
-
hepatocellular clear cell carcinoma
Keytruda
Orphan Designation
-
malignant carotid body paraganglioma
Keytruda
Orphan Designation
-
mediastinal malignant lymphoma
Keytruda
Orphan Designation
-
multisystemic smooth muscle dysfunction syndrome
Keytruda
Orphan Designation
-
nasopharyngeal carcinoma
pembrolizumab
Orphan Designation
-
natal teeth-intestinal pseudoobstruction-patent ductus syndrome
Keytruda
Orphan Designation
-
nut midline carcinoma
Keytruda
Orphan Designation
-
pediatric acute-onset neuropsychiatric syndrome
Keytruda
Orphan Designation
-
pediatric hepatocellular carcinoma
Keytruda
Orphan Designation
-
pediatric ovarian dysgerminoma
Keytruda
Orphan Designation
-
pediatric ovarian germ cell tumor
Keytruda
Orphan Designation
-
pediatric-onset Graves disease
Keytruda
Orphan Designation
-
post-treatment Lyme disease syndrome
Keytruda
Orphan Designation
-
primary adult heart tumor
Keytruda
Orphan Designation
-
primary mediastinal large B-cell lymphoma
Keytruda
Orphan Designation
-
small cell lung carcinoma
Keytruda
Orphan Designation
-
squamous carcinoma in situ
Keytruda
Orphan Designation
-
stage II endometrioid carcinoma
Keytruda
Orphan Designation
-
stage IVb bladder cancer
Keytruda
Orphan Designation
-
thymic neuroendocrine tumor
Keytruda
Orphan Designation
-
trabecular adenocarcinoma
Keytruda
Orphan Designation
-
treatment-refractory schizophrenia
Keytruda
Orphan Designation
-
uterine cervix carcinoma in situ
Keytruda
Orphan Designation
-
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