3
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| 8p inverted duplication/deletion syndrome | Human immunodeficiency virus immune globulin | Orphan Designation | - |
| AIDS | Human immunodeficiency virus immune globulin | Orphan Designation | - |
| ALG9-congenital disorder of glycosylation | Human immunodeficiency virus immune globulin | Orphan Designation | - |
| Au-Kline syndrome | Human immunodeficiency virus immune globulin | Orphan Designation | - |
| PURA-related severe neonatal hypotonia-seizures-encephalopathy syndrome | Human immunodeficiency virus immune globulin | Orphan Designation | - |
| monosomy X | Human immunodeficiency virus immune globulin | Orphan Designation | - |
| mosaic monosomy X | Human immunodeficiency virus immune globulin | Orphan Designation | - |