1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| LIPE-related familial partial lipodystrophy | N-acetyl-procainamide | Orphan Designation | - |
| gastrointestinal stromal tumor | N-acetyl-procainamide | Orphan Designation | - |
| lice infestation | N-acetyl-procainamide | Orphan Designation | - |