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Nat'l Tay-Sachs & Allied Diseases Association — Rare Disease Pipeline | Kisho | Kisho
Nat'l Tay-Sachs & Allied Diseases Association
Other
1
Orphan Designations
0
FDA Approvals
1
Rare Diseases
0
News Articles
Pipeline
Designations
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Diseases
Disease
Drug(s)
Designation
Approved
Sandhoff disease
recombinant adeno- associated virus vector AAV2/rh8 expressing human B-hexosaminidase A and B subunits
Orphan Designation
-
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