2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Alstrom syndrome | bempegaldesleukin | Orphan Designation | - |
| Finnish type amyloidosis | bempegaldesleukin | Orphan Designation | - |
| lysinuric protein intolerance | bempegaldesleukin | Orphan Designation | - |
| ovarian cancer | etirinotecan pegol | Orphan Designation | - |