1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| basal ganglia calcification, idiopathic, childhood-onset | Pioglitazone hydrochloride | Orphan Designation | - |
| childhood-onset dementia | Pioglitazone hydrochloride | Orphan Designation | - |
| childhood-onset idiopathic generalized epilepsy syndrome | Pioglitazone hydrochloride | Orphan Designation | - |