1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute disseminated encephalomyelitis | VALTOCO | Orphan Designation | - |
| acute flaccid myelitis | VALTOCO | Orphan Designation | - |
| acute lymphoblastic leukemia | VALTOCO | Orphan Designation | - |
| acute myeloid leukemia | VALTOCO | Orphan Designation | - |
| developmental and epileptic encephalopathy 119 | VALTOCO | Orphan Designation | - |
| febrile infection-related epilepsy syndrome | VALTOCO | Orphan Designation | - |