1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| developmental and epileptic encephalopathy, 24 | Melatonin | Orphan Designation | - |
| intellectual disability, autosomal dominant 24 | Melatonin | Orphan Designation | - |
| non-24-hour sleep-wake syndrome | Melatonin | Orphan Designation | - |