2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Floating-Harbor syndrome | Autologous Osteogenic Stem Cells | Orphan Designation | - |
| congenital pseudoarthrosis of the tibia | autologous osteogenic cells cultured from adipose tissue derived stem cells embedded in extracellular matrix with demineralized bone matrix. | Orphan Designation | - |
| phocomelia, Schinzel type | Autologous Osteogenic Stem Cells | Orphan Designation | - |
| restrictive dermopathy 1 | Autologous Osteogenic Stem Cells | Orphan Designation | - |