2
Orphan Designations
0 approved, 2 designated
0
FDA Approvals
0
Active Trials
200 recruiting
4
Rare Diseases
across 7 areas
0
News (30d)
Quiet
NuvOx Pharma is a company with 2 orphan drug designations across 4 rare diseases. gene therapy candidates in 1 disease. 19 active policy bills affect their portfolio.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| adult spinal cord glioblastoma | dodecafluoropentane emulsion (DDFPe) | Des.TrialAppr. |
| brain glioblastoma | dodecafluoropentane emulsion (DDFPe) | Des.TrialAppr. |
| glioblastoma | dodecafluoropentane emulsion (DDFPe) | Des.TrialAppr. |
| sickle cell disease | dodecafluoropentane emulsion | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
9
overlap in 2+ diseases
1/4
candidate diseases
0
avg importance: 0
19
affecting portfolio
0% of portfolio targets high unmet need diseases
9
overlap in 2+ diseases
1/4
candidate diseases
0
avg importance: 0
19
affecting portfolio