3
Orphan Designations
0
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Down syndrome | Gleolan | Orphan Designation | - |
| GM1 gangliosidosis | Gleolan | Orphan Designation | - |
| Jaberi-Elahi syndrome | Gleolan | Orphan Designation | - |
| Woodhouse-Sakati syndrome | Gleolan | Orphan Designation | - |
| hereditary breast ovarian cancer syndrome | Gleolan | Orphan Designation | - |
| leukoencephalopathy with vanishing white matter | Gleolan | Orphan Designation | - |
| neurodegeneration, childhood-onset, with ataxia, tremor, optic atrophy, and cognitive decline | Gleolan | Orphan Designation | - |
| ovarian cancer | Gleolan | Orphan Designation | - |
| ovarian neuroendocrine neoplasm | Gleolan | Orphan Designation | - |
| primary peritoneal carcinoma | Gleolan | Orphan Designation | - |
| spatial visualization, aptitude for | Gleolan | Orphan Designation | - |