1
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Ehlers-Danlos syndrome, vascular type | Cafcit | Orphan Designation | - |
| Meier-Gorlin syndrome 4 | Cafcit | Orphan Designation | - |
| Myhre syndrome | Cafcit | Orphan Designation | - |
| Ogden syndrome | Cafcit | Orphan Designation | - |
| Silver-Russell syndrome 5 | Cafcit | Orphan Designation | - |
| Tessadori-Van Haaften neurodevelopmental syndrome 3 | Cafcit | Orphan Designation | - |
| apnea of prematurity | Cafcit | Orphan Designation | - |
| early congenital syphilis | Cafcit | Orphan Designation | - |
| infantile apnea | Cafcit | Orphan Designation | - |