1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Alstrom syndrome | fialuridine | Orphan Designation | - |
| COG8-congenital disorder of glycosylation | fialuridine | Orphan Designation | - |
| Sjogren syndrome | fialuridine | Orphan Designation | - |