1
Orphan Designations
1
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Angelman syndrome | Cytalux | Orphan Designation | - |
| acute sensory ataxic neuropathy | Cytalux | Orphan Designation | - |
| aortic valve disease 1 | Cytalux | Orphan Designation | - |
| aortic valve stenosis | Cytalux | Orphan Designation | - |
| ovarian cancer | Cytalux | Orphan Designation | - |