1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| B-cell acute lymphoblastic leukemia | autologous T-cells ex vivo modified with a lentiviral vector encoding a chimeric antigen receptor specific for CD1a | Orphan Designation | - |
| acute lymphoblastic leukemia | autologous T-cells ex vivo modified with a lentiviral vector encoding a chimeric antigen receptor specific for CD1a | Orphan Designation | - |
| precursor T-cell acute lymphoblastic leukemia | autologous T-cells ex vivo modified with a lentiviral vector encoding a chimeric antigen receptor specific for CD1a | Orphan Designation | - |