1
Orphan Designations
1
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| interstitial lung disease due to ABCA3 deficiency | Infasurf | Orphan Designation | - |
| surfactant metabolism dysfunction, pulmonary, 1 | Infasurf | Orphan Designation | - |
| surfactant metabolism dysfunction, pulmonary, 2 | Infasurf | Orphan Designation | - |