1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| RFT1-congenital disorder of glycosylation | long acting recombinantFactor VIIa-CTP3 | Orphan Designation | - |
| Stormorken syndrome | long acting recombinantFactor VIIa-CTP3 | Orphan Designation | - |
| sitosterolemia 1 | long acting recombinantFactor VIIa-CTP3 | Orphan Designation | - |