2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bloom syndrome | 6-mercaptopurine oral liquid | Orphan Designation | - |
| Dubowitz syndrome | 6-mercaptopurine oral liquid | Orphan Designation | - |
| acute lymphoblastic leukemia | methotrexate | Orphan Designation | - |
| glioma susceptibility 3 | 6-mercaptopurine oral liquid | Orphan Designation | - |