4
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| intellectual disability-spasticity-ectrodactyly syndrome | L-baclofen | Orphan Designation | - |
| intractable diarrhea-choanal atresia-eye anomalies syndrome | L-baclofen | Orphan Designation | - |
| microcephaly-brain defect-spasticity-hypernatremia syndrome | L-baclofen | Orphan Designation | - |
| myoclonus, intractable, neonatal | L-baclofen | Orphan Designation | - |
| refractory celiac disease | L-baclofen | Orphan Designation | - |
| spasticity-ataxia-gait anomalies syndrome | L-baclofen | Orphan Designation | - |
| trigeminal neuralgia | L-baclofen | Orphan Designation | - |