1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bethlem myopathy 1A | Dehydroepiandrosterone (DHEA) | Orphan Designation | - |
| cardiomyopathy, familial hypertrophic, 31 | Dehydroepiandrosterone (DHEA) | Orphan Designation | - |
| congenital myopathy 26 | Dehydroepiandrosterone (DHEA) | Orphan Designation | - |