2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| lymphatic malformation | sirolimus | Orphan Designation | - |
| lymphatic malformation 5 | sirolimus | Orphan Designation | - |
| lymphatic malformation 6 | sirolimus | Orphan Designation | - |
| pachyonychia congenita | sirolimus | Orphan Designation | - |