2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| mucopolysaccharidosis type 1 | pentosan polysulfate | Orphan Designation | - |
| mucopolysaccharidosis type 6 | pentosan polysulfate sodium | Orphan Designation | - |
| mucopolysaccharidosis type 6, rapidly progressing | pentosan polysulfate sodium | Orphan Designation | - |
| mucopolysaccharidosis type 7 | pentosan polysulfate sodium | Orphan Designation | - |