1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| chromosome 17q23.1-q23.2 deletion syndrome | sodium dichloroacetate | Orphan Designation | - |
| hydrops-lactic acidosis-sideroblastic anemia-multisystemic failure syndrome | sodium dichloroacetate | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 13 | sodium dichloroacetate | Orphan Designation | - |