3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Beemer-Langer syndrome | amikacin sulfate | Orphan Designation | - |
| brain-lung-thyroid syndrome | amikacin sulfate | Orphan Designation | - |
| cranioectodermal dysplasia 2 | amikacin sulfate | Orphan Designation | - |
| hereditary hemorrhagic telangiectasia | thalidomide | Orphan Designation | - |
| mesothelioma | Cisplatin loaded hyaluronate film for implant | Orphan Designation | - |