1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Alstrom syndrome | Polyvalent, shed-antigen melanoma vaccine | Orphan Designation | - |
| Finnish type amyloidosis | Polyvalent, shed-antigen melanoma vaccine | Orphan Designation | - |
| lysinuric protein intolerance | Polyvalent, shed-antigen melanoma vaccine | Orphan Designation | - |