2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| compensatory emphysema | Transgenic human alpha 1 antitrypsin | Orphan Designation | - |
| cystic fibrosis | recombinant human alpha-1 antitrypsin | Orphan Designation | - |
| emphysema, hereditary pulmonary | Transgenic human alpha 1 antitrypsin | Orphan Designation | - |
| pulmonary emphysema | Transgenic human alpha 1 antitrypsin | Orphan Designation | - |